Advanced Medicine

Ophthalmology is quietly becoming gene therapy’s next big frontier. Here’s how the science, the patients, and the regulations are aligning.

Our latest news roundup reports on CAR t cell therapy at J&J and a second patient death linked to a Sarepta gene therapy.

Our latest news roundup reports on dysfunction observed in edited blood stem cells, and RFK Jr’s support for experimental treatments.

Stanford University researchers explore how zinc fingers can enhance gene therapy.

The IQVIA Institute’s latest report evaluates how well seven countries are prepared to support the complex infrastructure required for CAR T therapies

Our latest news roundup reports on a cell therapy facility expansion in Princeton, a magnet to capture T cells, and more.

Work from the lab of Luigi Naldini identifies postnatal window for in vivo gene editing, without the need for conditioning or transplantation

Patient fatality reported in clinical trial for investigational gene therapy for Danon disease.

Our latest news roundup reports on a gene therapy for Duchenne muscular dystrophy that can be re-dosed, a free toolkit for gene delivery, and more.

Researchers conduct small phase I study on placenta-derived stem cell therapy to treat a serious form of multiple sclerosis